Prenatal SMA treatment improved weight, movement, muscle health and survival in mice, but some benefits faded after therapy ...

The European decision on Scholar Rock’s SMA treatment apitegromab will depend on upcoming FDA results from a U.S. plant ...

Serving as her friend Andrea's maid of honor enabled columnist Connie Chandler to reciprocate the kind of care Andrea always ...

A Spinraza treatment pause during pregnancy was followed by mild motor decline and partial recovery postpartum. SMA treatment decisions during pregnancy require individualized assessment based on ...

Connie Chandler is a Christ-focused care and support specialist at the nonprofit organization Joni and Friends. She grew up in the foothills of North Carolina but now owns a home and lives in Fort ...

Alyssa Silva is a writer based out of Providence, Rhode Island. She was diagnosed with SMA type 1 in 1991 when she was just 5 months old. Aside from writing, Alyssa is the chief creative officer for ...

We are pleased to partner with the Muscular Dystrophy Association (MDA) to bring you coverage from the MDA Engage Symposium.