The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Merck KGaA agreed to a deal with RNA biotech Skyhawk Therapeutics that could top out at $2 billion. Roche’s Genentech terminated a cell therapy partnership with Adaptive Biotechnologies, ending what ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has approved ...

As aging progresses, the quality of DNA and proteins inside cells declines, which is known to be the cause of various ...

In the past decade there has been significant interest in studying the expression of our genetic code down to the level of ...

The collaboration will explore RNA-based small molecule drug candidates aimed at neurological conditions where existing ...